The Institute of Biotherapies coordinates transversal projects, in particular the development of four laboratories: The Institute of Myology, Genethon, I-Stem and Atlantic Gene therapies. The projects, which are developed internally or in partnership, involve pathologies of the neuromuscular, ocular, and immune systems, diseases related to aging, and other pathologies.
- Muscle diseases
- Duchenne muscular dystrophy
- Type 2 myotonic dystrophy
- Type I myotonic dystrophy—Steinert’s disease
- Becker muscular dystrophy
- Facioscapulohumeral Dystrophy
- Hereditary Inclusion Body Myopathy
- Myotubular myopathy
- Sporadic Inclusion Body Myositis
- GSDII or Pompe Disease
- SMA-spinal muscular atrophies
- Glycogen storage disease III—metabolic muscular dystrophy
- Dysferlinopathies
- Blood disorders
- Hereditary Skin Diseases
- Neurologic and Brain Diseases
- Diseases of the eye
- Diseases of the heart
- Premature aging diseases
- Liver Diseases
- Other diseases
