Cure through innovation
Breaking news
- 20 April 2021 Duchenne Muscular Dystrophy : First child dosed in Clinical Trial of Investigational Gene therapy
- 2 June 2020 A Genethon team has succeeded in inhibiting the immune response linked to AAV
- 25 June 2019 CRISPR-Cas9 : First in vivo proof-of-concept in Steinert’s myotonic dystrophy, a neuromuscular disease
- 4 June 2019 The first FDA-approved gene therapy for a neuromuscular disease in the United States is a wonderful hope for patients, also a key challenge for France
- 29 May 2019 Gene therapy : Towards a clinical trial for gamma-sarcoglycanopathy, limb-girdle muscular dystrophy
- 25 February 2019 Treatment of X-CGD : positive results of the gene therapy initiated by Genethon
