ASGCT 2026: Genethon presents results from three gene therapy programs in clinical development

At ASGCT 2026 in Boston, Genethon presented new clinical data from three of its gene therapy programs in Duchenne muscular dystrophy, gamma-sarcoglycanopathy (LGMD-R5), and Crigler-Najjar syndrome. In total, Genethon teams presented 8 oral presentations and 13 posters.

Genethon, the French laboratory dedicated to the research and development of gene therapies for rare diseases created by AFM-Telethon, presented several clinical results at the annual meeting of the American Society of Gene & Cell Therapy (ASGCT), held from May 11 to 15, 2026, in Boston, USA.

Genethon teams presented a total of 8 oral presentations and 13 posters covering several gene therapy programs currently in clinical development.

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